20/07/2026Veri Anla Niemann-Pick type C ni ugonjwa wa kurithi wenye neurodegeneration unaotokana na mkusanyiko usiofaa wa kolesteroli kwenye lysosomes. HP-β-CD huchunguzwa kwa uwezo wake wa kuyeyusha na kupunguza mkusanyiko huu, lakini ni mchanganyiko wa molekuli zenye degrees of substitution tofauti. Tazama zaidi
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